Gene Therapies for ALS, Friedreich’s Ataxia the Focus of New CRISPR, Capsida Partnership

The news comes after CRISPR’s favorable data readouts in its sickle cell and beta thalassemia studies.

Mesenchymal Stem Cells Hold Promise for Osteoarthritis and More Chronic Diseases

Cynata Therapeutics' Ross Macdonald, PhD, discusses the company's pipeline and clinical-phase trials.

KTE-X19 Safe, Efficacious as Therapy for Pediatric B-Cell ALL in ZUMA-4

Results of the phase 1 portion of ZUMA-4 support continued investigation into the efficacy of KTE-X19 in pediatric patients with B-cell acute lymphoblastic leukemia.

Cilta-cel for the Treatment of Multiple Myeloma: Mounzer Agha, MD

The director of the Mario Lemieux Center for Blood Cancers at UPMC Hillman Cancer Center discussed findings from the CARTITUDE studies.

Targeting Human Retinal Progenitor Cell Injections for Retinitis Pigmentosa

Investigators find approach improved vision and visual fields in some patients.

Axi-cel Shows Efficacy, Durability, in Relapsed/Refractory Follicular Lymphoma

Henry Chi Hang Fung, MD, from the Fox Chase Cancer Center, discusses axi-cel's potential in relapsed/refractory FL.