Addressing Unmet Needs With Gene Therapy

Eric Crombez, PhD, senior vice president and chief medical officer of Ultragenyx Gene Therapy, discussed indications the company is targeting.

Gene Therapy for Retinal and Neurological Diseases

Magali Taiel, MD, chief medical officer, GenSight Biologics, discussed future research the company plans to pursue.

Severe Neurodegenerative, Epileptic Disorders the Target of Taysha Gene Therapies

With numerous targets in CNS diseases and a unique partnership with gene therapy experts at UT Southwestern, Taysha is hoping to fill significant unmet needs.